The AGAMREE SUMMIT Study joins other important research opportunities studying DMD, offering the benefits of an observational registry with the inclusion of state-of-the-art imaging and data collection. The study will follow 250 participants who are taking AGAMREE for the treatment of DMD for up to 5 years. Healthcare providers at 25 sites across the United States will gather a wide range of information from participants. Along with supplementing existing DMD research with real-world information, the main focus of the AGAMREE SUMMIT Study is to better understand outcomes associated with long-term AGAMREE treatment, including bone health, behavior, sexual development, and cataract formation.
- Participants will be followed for approximately 5 years and will be expected to return to the study site for yearly follow-up visits.
- Participants may receive travel assistance depending on the distance from the study site.
- Participants will receive a physical examination at each visit, and blood work and state-of-the-art imaging tests may be conducted.
- There will be no cost to participants in the study—the study will pay for all out-of-pocket expenses associated with procedures (physical exams,
blood draws, study scans, etc.).
- There will be no cost to participants in the study—the study will pay for all out-of-pocket expenses associated with procedures (physical exams,
- Quality-of-life questionnaires will also be completed at each return visit.
- All members of the DMD community understand the importance of research. By participating in the AGAMREE SUMMIT Study, your family will provide important
data that may be helpful in developing better treatment options for DMD patients in the future.
- Participants in SUMMIT must be at least 2 years old, have received a confirmed diagnosis of DMD, and be currently taking AGAMREE. Participants or their parent/
legal guardian (for those younger than 18 years old) must provide written informed consent after hearing about the AGAMREE SUMMIT Study and be willing to
complete quality-of-life questionnaires.
Ask your healthcare provider about the
AGAMREE SUMMIT Study during your next appointment
For more information, contact Nadeem Khaliq, MBBS (MD) at Nadeem.Khaliq@catalystpharma.com
Note: Not all care centers are participating in the AGAMREE SUMMIT Study.